FDA announces landmark approval of gene therapy for inherited retinal dystrophies

A suite of formerly untreatable, progressively blinding retinal diseases may now be halted or even reversed, thanks to FDA approval of the gene therapy agent, Luxturna. The announcement marks the first U.S. approval of a gene therapy for an inherited disease.
Source: Daily Dose of Eye Care

https://www.lvcenter4sight.com/fda-announces-landmark-approval-of-gene-therapy-for-inherited-retinal-dystrophies/

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